FDA approves first gene-editing treatment for human illness
Dec 8, 2023 · The Food and Drug Administration approved two genetic treatments for sickle cell disease, including one that uses gene-editing. The approvals offer hope for patients and signal a new medical era.
What is CRISPR? A bioengineer explains | Stanford Report
Jun 10, 2024 · The short answer: CRISPR is an immune system used by microbes to find and eliminate unwanted invaders. Qi: CRISPR stands for “clustered interspaced short palindromic repeats.” Biologists use ...
FDA approves cure for sickle cell disease, the first ...
Dec 8, 2023 · The therapy, called Casgevy, from Vertex Pharmaceuticals and CRISPR Therapeutics, is the first medicine to be approved in the United States that uses the gene-editing tool CRISPR, which won its...
The world's 1st CRISPR therapy has been approved. Here's ...
Jan 18, 2024 · Drug regulators have approved a CRISPR therapy called Casgevy to treat inherited blood disorders. But what is it and how does it work?
CRISPR 2.0: a new wave of gene editors heads for clinical trials
Dec 7, 2023 · Less than a month after the world’s first approval of a CRISPR–Cas9 genome-editing therapy, researchers are hoping that the therapy will win its second authorization this week — this time...
FDA Approves First CRISPR Treatment in U.S. | TIME
Dec 8, 2023 · CRISPR can increase the population of healthy blood cells in both groups of patients. The FDA approved exa-cel for sickle cell disease, and will make a decision about treating beta thalassemia by...
Gene-editing treatment for sickle cell appears headed for FDA ...
Oct 31, 2023 · A committee of independent FDA advisers Tuesday praised the treatment, which uses the gene-editing technique called CRISPR to treat sickle cell disease, a devastating blood disorder. The...