Research into new bandaging aims to ease the agony experienced by those living with genetic skin condition Epidermolysis Bullosa (EB), commonly referred to as 'butterfly skin'.
A Phase 2 trial testing oral ROCK inhibitor Bravyl in people with ALS is now fully enrolled at its highest dosing group.
SMA treatment Spinraza followed by Zolgensma improved motor function and prevented worsening of breathing difficulties in a ...